The DMD gene produces dystrophin, a protein that maintains the structure of muscle cells. People with DMD have mutations (changes) in the gene that cause a loss of dystrophin protein in cells.

Multiparametric quantitative MRI could potentially help differentiate between Duchenne muscular dystrophy and Becker muscular dystrophy early and improve the management of these conditions.

In male patients with DMD, treatment with deramiocel reduced upper limb function deterioration compared ... 014). Improvements in cardiac function and structure were also noted in the deramiocel group ...

Presentation Details: Title: ARCUS-Mediated Excision of Exons 45-55 Leads to Functional Del45-55 Dystrophin and Restoration of Skeletal Muscle-Function for the Treatment of DMD Date and Time ...