Childhood-onset striatonigral degeneration is a rare genetic disorder that robs children of the ability to walk and speak by ...

A rare virus that killed actor Gene Hackman's wife in February has been linked to the deaths of three people in California.

Three people in the rural California town of Mammoth Lakes have died from the same rare virus that killed Gene Hackman’s wife ...

A federal advisory committee that provides guidance on which rare diseases newborns should be screened for has been dissolved ...

None of the cell and gene therapies that reached the final regulatory submission stage were rejected by the FDA.

Three people are dead from the same virus that killed Gene Hackman's wife, Betsy Arakawa, sparking concern among local ...

Eleven foals in the Pacific Northwest were diagnosed with a condition called Equine Juvenile Spinocerebellar Ataxia (EJSCA).

A surprising mix of inherited and de novo mutations in 60 genes contribute to 10 percent of CHD cases. Many of these same ...

Hantavirus – the virus that causes hantavirus pulmonary syndrome (HPS) and took the life of Gene Hackman's wife Betsy – has ...

Swedish researchers have identified genetic variants that increase the risk of atherosclerosis. The aim is for these new ...

The $150 million will also go toward Atsena’s preclinical pipeline and expand the use of the biotech’s spreading AAV.SPR ...