Alternative splicing is crucial for eukaryotic gene expression and influences protein function and regulation, with mis-splicing linked to numerous diseases. In this webinar, Dr. Megan L Noonan will ...
although because this study was not based on a data set of whole genomic DNA for each gene, the background of incomplete splicing/pre-mRNA contamination could not be fully assessed. Similar ...
Splicebio S.L. has gained IND clearance from the FDA for its lead program SB-007, a protein splicing gene therapy to address the root genetic cause of Stargardt disease. The company plans to initiate ...