Gene therapy reverses symptoms of rare neurological disease in animal models
A recent study led by the UAB demonstrates the potential of gene therapy to restore motor capacity in an ultra-rare disease, ...
Gene editing with adeno-associated virus vector offers hope for hereditary deafness
An R75W mutation in the gap junction β2 (GJB2) gene causes severe fragmentation of gap junction plaques, connecting adjacent ...
Zacks Investment Research on MSN13 小时
PCRX Doses First Patient in Phase II PCRX-201 Gene Therapy Study
Pacira BioSciences PCRX announced that it has dosed the first patient in a mid-stage study of pipeline candidate PCRX-201 ...
Technology Networks4 天
Gene Therapy Restores Motor Capacity in Animal Models of Rare Neurological Disease
A recent study demonstrated the potential of gene therapy to restore motor capacity in an ultra-rare disease, megalencephalic ...
The Munich Eye2 天
New Atlas Reveals Optimal Viral Vectors for Gene Therapy Applications
Munich news, health insurance, technology, jobs and other topics for expatriates. The Eye Newspapers covers daily news and offers services for foreigners.
News-Medical.Net on MSN8 天
Transforming genetic deafness treatment with base editing
Congenital hearing loss refers to impaired auditory function that occurs due to genetic causes. GJB2 is the gene responsible ...
EurekAlert!8 天
New study reveals the curative potential of genome editing approach for genetic deafness
R75W mutation in the gap junction β2 (GJB2) gene causes severe fragmentation of gap junction plaques, connecting adjacent ...
GEN - Genetic Engineering and Biotechnology News2 天
Digital Twin Focuses on Improving Viral Vector Production
The combination of synchronous experimental process development and digital twin core model development is among the first of its kind.
Mirage News4 天
Gene Therapy Reverses Rare Neurological Disease In Animals
A recent study led by the UAB demonstrates the potential of gene therapy to restore motor capacity in an ultra-rare disease, ...