Currently, the DMD treatment landscape includes Sarepta’s Elevidys (delandistrogene moxeparvovec), the first FDA-approved ...

Intrathecal delivery could kickstart sales of Zolgensma, which have taken a while to get going but did rise 69% to $634 million in the first half of the year, setting it on course for blockbuster ...

Broadly, access to the spinal cord may be achieved through one of two primary routes for delivery of a cellular graft: intrathecal; or direct microinjection. Intrathecal delivery refers to ...

Novartis intrathecal onasemnogene abeparvovec phase III STEER study meets primary endpoint in children and young adults with SMA: Basel Tuesday, December 31, 2024, 11:00 Hrs [IST] ...

Novartis has an exclusive, worldwide license with Nationwide Children's Hospital to both the intravenous and intrathecal delivery of adeno-associated virus 9 (AAV9) gene therapy for the treatment of ...