资讯
A new article argues dystrophin immunogenicity is an under-examined issue in the treatment of Duchenne muscular dystrophy.
Becker muscular dystrophy occurs when there’s a change or mutation in the gene that produces the protein dystrophin. The mutation can happen randomly or be passed down from your parents.
Global Duchenne Muscular Dystrophy Drugs Market value attained USD 3.9 Billion in 2025. The market will achieve USD 6.5 ...
Duchenne muscular dystrophy is characterized by a mutation in the DMD gene that leads to a lack of dystrophin and muscle loss. It affects about one in 3,300 boys. Delandistrogene moxeparvovec ...
Sarepta Therapeutics said Tuesday that a patient died while taking its closely watched gene therapy for muscular dystrophy, sending company shares plummeting more than 25%. A recent study ...
In June 2024, the FDA approved the labeled indication for Elevidys to include individuals with Duchenne muscular dystrophy who have a confirmed mutation in the DMD gene and are at least four years ...
Suneel Ram is a spiritual seeker, sings in a band and was the subject of a comic novel two years ago about living with Duchenne muscular dystrophy, a rare genetic ...
ELEVIDYS is indicated for the treatment of Duchenne muscular dystrophy (DMD) in individuals at least 4 years of age. For patients who are ambulatory and have a confirmed mutation in the DMD gene ...
Sarepta Therapeutics, Inc. (NASDAQ:SRPT), the leader in precision genetic medicine for rare diseases, shared the following ...
一些您可能无法访问的结果已被隐去。
显示无法访问的结果