The X-Men are some of the most powerful heroes in Marvel lore, but even icons like Cyclops and Colossus have siblings who ...

An SCD patient in Bahrain received the gene-editing therapy Casgevy, marking the first time the treatment has been given outside the U.S.

A man in his 70s from Oklahoma could provide a key to Alzheimer's disease, as scientists are rethinking the underlying cause of the condition and how it can be treated ...

A man in Oklahoma could be the missing piece scientists were looking for on the battle to prevent Alzheimer's disease.

Five oculopharyngeal muscular dystrophy (OPMD) patients have now been treated with the gene therapy candidate BB-301 in a ...

First patient dosed in the pediatric cohort of the Phase 1/2 trial of OPGx-LCA5; initial data on the cohort anticipated by Q3 2025New 12-month ...

Edneide Melo was 39 years old when she woke up in a hospital room in Brazil. But to her, it was 2003, and she was 25. She had ...

Ovarian cancer is one of the most common types of cancer in women, but the symptoms can be difficult to spot as they're often associated with other conditions. Here are the 10 warning signs to be ...

Edneide Melo was just 39 when she woke up from a routine operation - and found she'd lost 14 years of memories.

Edneide Melo woke up in a hospital room completely disoriented, and was horrified to discover her life had moved on in the 14 ...

Test your knowledge of spinal muscular atrophy (SMA) with this quiz covering its genetic causes, diagnosis, and treatment ...

Vincent Gaynor remembers, almost to the minute, when he realized his part in birthing the breakthrough gene therapy Zolgensma ...