Speakers from the Muscular Dystrophy Association (MDA) highlighted 75 years of progress in understanding and treating ...

The company plans to submit a biologics licence application to the US Food and Drug Administration later this year.

A young person with Duchenne muscular dystrophy died following treatment with the recently approved gene therapy ...

An 8-year-old northern Minnesota boy is one of the first in the country to receive a specific type of gene therapy treatment.

Precision BioSciences (DTIL) announced the presentation of preclinical data for its PBGENE-DMD development program for the treatment of ...

A patient has died while taking a closely watched gene therapy for muscular dystrophy. Sarepta Therapeutics announced the ...

Having found that in biomedical research, the Bird Rock resident and scientist at La Jolla’s Sanford Burnham Prebys has ...

Study results support the role of functional dystrophin and suggest that delandistrogene moxeparvovec stabilizes or slows ...

Avidity Biosciences’ Phase I/II trial of ribonucleic acid (RNA) therapy, del-zota, has increased dystrophin in patients with Duchenne muscular dystrophy (DMD). Results from the company’s ...

Peptris Technologies out-licenses India’s first AI discovered drug candidate to Revio Therapeutics: Our Bureau, Bengaluru Monday, March 17, 2025, 12:50 Hrs [IST] Peptris Technol ...