With the modality now in early clinical trials, experts say more efficiency, broader editing capabilities and delivery ...

The clinical features of MAS overlap with those of active sJIA, complicating early diagnosis and treatment. We evaluated adenosine deaminase 2 (ADA2), a protein of unknown function released ...

Telethon Foundation is seeking approval for a gene therapy to treat the rare disease Wiskott-Aldrich syndrome.

After hours: February 21 at 5:37:37 PM EST Loading Chart for ROIV ...

It previously did so with simoladagene autotemcel, a therapy for adenosine deaminase severe combined immunodeficiency (ADA-SCiD). That gene therapy also originated in the laboratories of the San ...

Transposable elements (TEs, transposons) are mobile DNAs that are prevalent in most eukaryotic genomes. In plants, their mobility has vastly contributed to genetic diversity which is essential for ...

Viral epidemiology is the scientific discipline concerned with the study of the incidence and spread of viruses in populations over time. Host, virus and environmental factors are monitored to ...

There is no rise in lactate due to complete failure of glycogen breakdown in muscles. An increased reliance on purine nucleotide metabolism (via myoadenylate deaminase) and phosphocreatine hydrolysis ...