Vincent Gaynor remembers, almost to the minute, when he realized his part in birthing the breakthrough gene therapy Zolgensma ...

When even the most highly trained surgeons perform procedures on the retina—one of the smallest, most delicate parts of the ...

The introduction of anti-VEGF agents has revolutionized the field of medical retina care by reducing rates of vision loss and ...

Dec. 10, 2024 — In a single IV injection, a gene therapy targeting cBIN1 can reverse the effects of heart failure and restore heart function in a large animal model. The therapy increases the ...

A 31-year-old Sligo man who was functionally blind has got his sight back, after being treated with a new gene therapy at the ...

Patients who underwent bilateral treatment experienced a higher rate of clinically relevant recovery, the authors reported.

The five-year trial saw patients who received a single injection of Lumevoq sustaining clinical recovery in a rare condition ...

The US Food and Drug Administration (FDA) has granted Regenerative Medicine Advanced Therapy (RMAT) designation to AskBio’s investigational Parkinson’s disease (PD) gene therapy. The FDA grants RMAT ...

This article examines viral and non-viral vectors in gene therapy, highlighting their mechanisms, advantages, and limitations ...

Gene therapies to treat rheumatoid arthritis have evolved slowly, but one is ready to move into human trials and an ...