Vincent Gaynor remembers, almost to the minute, when he realized his part in birthing the breakthrough gene therapy Zolgensma ...

The five-year trial saw patients who received a single injection of Lumevoq sustaining clinical recovery in a rare condition ...

When even the most highly trained surgeons perform procedures on the retina-one of the smallest, most delicate parts of the human body-the stakes are high.

Dec. 10, 2024 — In a single IV injection, a gene therapy targeting cBIN1 can reverse the effects of heart failure and restore heart function in a large animal model. The therapy increases the ...

Recent innovations in DNA-modifying will revolutionize the treatment of many diseases and prompt crucial discussions.

The introduction of anti-VEGF agents has revolutionized the field of medical retina care by reducing rates of vision loss and ...

A 31-year-old Sligo man who was functionally blind has got his sight back, after being treated with a new gene therapy at the ...

A robotic device developed by University of Utah engineers allows eye surgeons to perform high-precision procedures on the retina, the fragile lining on the back of the eye that is less than a ...

A one-time injection of Lumevoq demonstrated sustained visual acuity improvements with a favorable safety profile at 5 years ...

Holdings announced the publication of results from the first-in-human interventional study to treat children with ...

Patients who underwent bilateral treatment experienced a higher rate of clinically relevant recovery, the authors reported.

AskBio’s gene therapy AB-1005 to treat Parkinson’s disease receives US FDA Regenerative Medicine Advanced Therapy designation: Berlin, Germany Thursday, February 20, 2025, 10: ...